The Ark
A blog about our science, the rare disease community and PerlQuests
Perlstein Lab Burn Rate 2015 (Q1-Q2+May)
Previously, we highlighted Perlstein Lab’s burn rate from 2014. We’ll revisit that...
Biologics and you
In our last post we talked specifically about orphan drugs that are small molecules....
Orphan drug prices and approvals
This post kicks off a series about drug prices in the orphan drug space. We initially...
Humanized yeast to the rescue
There are many research examples of yeast genes that were replaced by human orthologs...
April in tweets
In April we crossed the midway point of our Niemann-Pick C multi-model HTS campaign....
World Orphan Drug Congress recap
I attended my first World Orphan Drug Congress last week in Washington, D.C. It was a...
Data data everywhere
I recently went to a conference where there was a panel discussion titled ‘Data...
March in tweets
March marked the beginning of the third month of our NPC HTS campaign. Let's take a...
NPC in a dish
For those who have read our posts before and follow us on Twitter, you know we are...
A worm screen for Niemann-Pick C
It’s soon going to be one year since we started screening for drug candidates that...
Rare Disease Day 2015
On behalf of the PLab team, I would like to wish everyone a happy Rare Disease Day...
